Ice Bucket Challenge donations have helped fund promising ALS clinical trials, especially for "fast progressors"
There are currently only four drugs approved to help treat amyotrophic lateral sclerosis (ALS)
Researchers find four new drug candidates to tackle Huntington's disease
There is currently no approved treatment for the reversal of Huntington's disease
Here's why many CRISPR/Cas9 experiments could be wrong – and how to fix them
Researchers assumed that CRISPR was turning off genes. They shouldn't have
A new test for cystic fibrosis takes just two minutes and a scrape across the forehead
Availability of better tests could lead to earlier diagnosis, which is crucial for effective management of the disease
We can use genes to find serial killers, but how much more can they really tell us?
Using genetic data from over 100,000 individuals, it is now possible to do everything from finding genetic predictors of disease to tracking murderers
Haven't heard of RNA therapy yet? You will
After a decade of painstaking progress, the underdog is on the brink of treating a broad range of diseases
How inbred dogs help us learn about human diseases
Dogs are helping scientists figure out why our copper storage systems can go haywire
Carl Zimmer explores the mysteries and contradictions of genetics
In 'She Has Her Mother's Laugh,' Zimmer reveals the lawlessness of our genes
We still don't know all the consequences of gene manipulation
Genome meddling to cure diseases is often worth the risk, but nothing else is just yet
As a scientist, sometimes I understand too much about my brother's cystic fibrosis
My knowledge of his disease can be helpful, but also supremely frustrating
Scientists are trying to cure diseases by harnessing our own cells
New research on Rett syndrome, caused by a mutated gene, suggests a treatment to reverse some disease symptoms
A rare disease offers clues to how genes affect social behavior
Williams syndrome is helping scientists understand the roots of sociality
The Mother's Curse: how a French king’s legacy revealed a loophole in evolution
New research with roots in colonial Canada suggests new wrinkles in ideas of evolution
How CRISPR proteins work together to capture foreign DNA
A biologist writes the CRISPR explainer you've been looking for
Why 'designer babies' won't be here anytime soon
Human embryos are uniquely resistant to inserting foreign DNA via CRISPR